Clinical Trial Update: Biomarker Validation for Niemann-Pick Disease, Type C: Safety and Efficacy of N-Acetyl Cysteine [Phase 1, Phase 2]

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Summary

A Phase 1/2 clinical trial evaluating the safety and potential efficacy of N-acetylcysteine in Niemann-Pick disease Type C has completed, with results posted in…

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Diseases / indications

• Niemann-pick Disease Type

Drugs mentioned

• N-Acetyl-Cysteine (N-acetylcysteine)

Snippet

Sponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) | Conditions: Niemann-Pick Disease, Type C | Phase 1, Phase 2 | Status: COMPLETED | Results posted: 2012-07-12