Clinical Trial Update: Safety Study of Mini-dystrophin Gene to Treat Duchenne Muscular Dystrophy [Phase 1]

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Summary

Phase 1 safety study of a mini-dystrophin gene therapy for Duchenne Muscular Dystrophy has been completed.

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Diseases / indications

• Duchenne Muscular Dystrophy

Drugs mentioned

• Mini-dystrophin gene therapy (mini-dystrophin gene transfer)

Snippet

Sponsor: Nationwide Children's Hospital | Conditions: Duchenne Muscular Dystrophy | Phase 1 | Status: COMPLETED