Clinical Trial Update: Intrathecal Enzyme Replacement Therapy for Spinal Cord Compression in Mucopolysaccharidosis (MPS) I [Phase 1]

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Summary

A Phase 1 clinical trial evaluating intrathecal enzyme replacement therapy for spinal cord compression in Mucopolysaccharidosis type I was terminated.

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Diseases / indications

• Mucopolysaccharidosis Type
• Spinal Cord Compression

Drugs mentioned

• Intrathecal Enzyme Replacement Therapy

Snippet

Sponsor: Patricia I. Dickson, M.D. | Conditions: Mucopolysaccharidosis I, Lysosomal Storage Diseases | Phase 1 | Status: TERMINATED