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CLINICAL_TRIALS trial_result · 2024-06-10

Clinical Trial Update: A Study of Potential Treatment-Responsive Biomarkers and Clinical Outcomes in Hunter Syndrome

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Summary

Denali Therapeutics completed a clinical trial in Mucopolysaccharidosis type II investigating potential treatment-responsive biomarkers and clinical outcomes.

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Diseases / indications

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Sponsor: Denali Therapeutics Inc. | Conditions: Mucopolysaccharidosis II | Status: COMPLETED