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CLINICAL_TRIALS trial_result · 2012-04-13

Clinical Trial Update: Safety, Tolerability, and Activity Study of ISIS SOD1Rx to Treat Familial Amyotrophic Lateral Sclerosis (ALS) Caused by SOD1 Gene Mutations [Phase 1]

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Summary

Phase 1 study evaluating safety, tolerability, and activity of ISIS SOD1Rx in familial ALS caused by SOD1 mutations has completed.

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Diseases / indications

Drugs mentioned

  • ISIS SOD1Rx

Snippet

Sponsor: Ionis Pharmaceuticals, Inc. | Conditions: Familial Amyotrophic Lateral Sclerosis | Phase 1 | Status: COMPLETED