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CLINICAL_TRIALS trial_result · 2012-05-21

Clinical Trial Update: Safety and Pharmacokinetics of Sialic Acid Tables in Patients With Hereditary Inclusion Body Myopathy (HIBM) [Phase 1]

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Summary

Phase 1 study assessing safety and pharmacokinetics of Sialic Acid Tables in patients with Hereditary inclusion body myopathy has completed.

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Diseases / indications

Drugs mentioned

  • Sialic Acid Tables (sialic acid)

Snippet

Sponsor: Ultragenyx Pharmaceutical Inc | Conditions: Hereditary Inclusion Body Myopathy (HIBM) | Phase 1 | Status: COMPLETED