CLINICAL_TRIALS
trial_result
· 2012-05-21
Clinical Trial Update: Safety and Pharmacokinetics of Sialic Acid Tables in Patients With Hereditary Inclusion Body Myopathy (HIBM) [Phase 1]
Summary
Phase 1 study assessing safety and pharmacokinetics of Sialic Acid Tables in patients with Hereditary inclusion body myopathy has completed.
Upgrade for the full analysis, importance score, and drug timeline.
Diseases / indications
Drugs mentioned
Snippet
Sponsor: Ultragenyx Pharmaceutical Inc | Conditions: Hereditary Inclusion Body Myopathy (HIBM) | Phase 1 | Status: COMPLETED