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CLINICAL_TRIALS trial_result · 2024-01-03

Clinical Trial Update: Study of Safety, Efficacy, Tolerability, Pharmacokinetics and Pharmacodynamics of LNP023 in in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH) [Phase 2]

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Summary

Phase 2 trial evaluating LNP023 (iptacopan) for safety, efficacy, tolerability, pharmacokinetics, and pharmacodynamics in patients with paroxysmal nocturnal hem…

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Diseases / indications

Drugs mentioned

  • LNP023 (iptacopan)

Snippet

Sponsor: Novartis Pharmaceuticals | Conditions: Paroxysmal Nocturnal Hemoglobinuria (PNH) With Signs of Active Hemolysis | Phase 2 | Status: COMPLETED | Results posted: 2024-01-03