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CLINICAL_TRIALS trial_result · 2023-12-18

Clinical Trial Update: Efficacy, Safety, Pharmacokinetics and Pharmacodynamics Study, Assessing Multiple LNP023 Doses in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria [Phase 2]

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Summary

Phase 2 trial evaluating multiple doses of iptacopan (LNP023) in adults with paroxysmal nocturnal hemoglobinuria to assess efficacy, safety, PK and PD; results …

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Diseases / indications

Drugs mentioned

  • iptacopan (iptacopan)

Snippet

Sponsor: Novartis Pharmaceuticals | Conditions: Paroxysmal Nocturnal Hemoglobinuria | Phase 2 | Status: COMPLETED | Results posted: 2023-12-18