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CLINICAL_TRIALS trial_result · 2010-02-12

Clinical Trial Update: Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Types II or III [Phase 1, Phase 2]

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Summary

A phase 1/2 clinical trial evaluating sodium phenylbutyrate in children with spinal muscular atrophy types II and III was terminated, and results were posted in…

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Diseases / indications

Drugs mentioned

  • Sodium phenylbutyrate (sodium phenylbutyrate)

Snippet

Sponsor: Westat | Conditions: Spinal Muscular Atrophy Type II, Spinal Muscular Atrophy Type III | Phase 1, Phase 2 | Status: TERMINATED | Results posted: 2010-02-12