CLINICAL_TRIALS
research
· 2024-06-27
Clinical Trial Update: A Natural History Study of Neuronal Ceroid Lipofuscinosis Type 5 (CLN5)
Summary
This update reports the completion of a natural history (observational) study of Ceroid Lipofuscinosis, Neuronal 5 (CLN5).
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Diseases / indications
Snippet
Sponsor: Neurogene Inc. | Conditions: Ceroid Lipofuscinosis, Neuronal 5 | Status: COMPLETED