Clinical Trial Update: A Long-Term Study of Olipudase Alfa in Patients With Acid Sphingomyelinase Deficiency [Phase 2]

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Summary

This document reports long-term results from a Phase 2 study of olipudase alfa in patients with acid sphingomyelinase deficiency (Niemann-Pick disease types A a…

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Diseases / indications

• Acid Sphingomyelinase Deficiency
• Niemann-pick Disease Types and

Drugs mentioned

• XENPOZYME (olipudase alfa-RPCP)

Snippet

Sponsor: Genzyme, a Sanofi Company | Conditions: Sphingomyelin Lipidosis | Phase 2 | Status: COMPLETED | Results posted: 2024-07-03