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CLINICAL_TRIALS trial_result · 2024-07-03

Clinical Trial Update: A Long-Term Follow-Up Study of Participants With Cystinosis Who Previously Received CTNS-RD-04

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Summary

A long-term follow-up study is investigating outcomes in cystinosis patients who previously received CTNS-RD-04, with enrollment by invitation.

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Diseases / indications

Drugs mentioned

  • CTNS-RD-04

Snippet

Sponsor: Stephanie Cherqui | Conditions: Cystinosis | Status: ENROLLING_BY_INVITATION