CLINICAL_TRIALS
trial_result
· 2024-07-03
Clinical Trial Update: A Long-Term Follow-Up Study of Participants With Cystinosis Who Previously Received CTNS-RD-04
Summary
A long-term follow-up study is investigating outcomes in cystinosis patients who previously received CTNS-RD-04, with enrollment by invitation.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Stephanie Cherqui | Conditions: Cystinosis | Status: ENROLLING_BY_INVITATION