Clinical Trial Update: Gene Therapy for Gaucher's and Fabry Disease Using Viruses and Blood-Forming Cells [Phase 1]

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Summary

A Phase 1 clinical trial update on gene therapy for Gaucher disease and Fabry disease using viral vectors and blood-forming cells has completed, sponsored by NI…

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Diseases / indications

• Fabry Disease
• Gaucher Disease

Snippet

Sponsor: National Institute of Neurological Disorders and Stroke (NINDS) | Conditions: Gaucher's Disease | Phase 1 | Status: COMPLETED