Clinical Trial Update: Evaluation of the Safety, Tolerability and Efficacy of a Gene Therapy Drug for the Treatment of Pediatric Fabry Disease [EARLY_Phase 1]

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Summary

A Phase 1 pediatric trial is evaluating a gene therapy drug for Fabry disease, focusing on safety, tolerability, and efficacy. The study is currently recruiting…

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Diseases / indications

• Fabry Disease

Snippet

Sponsor: Children's Hospital of Fudan University | Conditions: Fabry Disease | EARLY_Phase 1 | Status: RECRUITING