Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS trial_result · 2006-11-03

Clinical Trial Update: Study of Recombinant Human N-Acetylgalactosamine 4-Sulfatase in Patients With MPS VI [Phase 1]

View source ↗

Summary

A Phase 1 clinical trial evaluating recombinant human N-acetylgalactosamine 4-sulfatase in patients with Mucopolysaccharidosis VI has completed.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • Elosulfase alfa (Arylsulfatase B)

Snippet

Sponsor: BioMarin Pharmaceutical | Conditions: Mucopolysaccharidosis VI | Phase 1 | Status: COMPLETED