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CLINICAL_TRIALS trial_result · 2024-07-22

Clinical Trial Update: Brain Involvement in Dystrophinopathies Part 2

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Summary

A completed clinical trial update on brain involvement in dystrophinopathies, including Duchenne muscular dystrophy and Becker muscular dystrophy.

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Diseases / indications

Snippet

Sponsor: Great Ormond Street Hospital for Children NHS Foundation Trust | Conditions: Duchenne Muscular Dystrophy, Becker Muscular Dystrophy | Status: COMPLETED