Clinical Trial Update: Investigate Safety, Tolerability, PK, PD and Efficacy of Risdiplam (RO7034067) in Infants With Type1 Spinal Muscular Atrophy [Phase 2]

View source ↗

Summary

A Phase 2 trial of risdiplam in infants with Spinal muscular atrophy completed, reporting safety, tolerability, PK/PD and efficacy with results posted in Januar…

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

• Spinal Muscular Atrophy

Drugs mentioned

• Risdiplam (risdiplam)

Snippet

Sponsor: Hoffmann-La Roche | Conditions: Muscular Atrophy, Spinal | Phase 2 | Status: COMPLETED | Results posted: 2021-01-08