Clinical Trial Update: Early Access Program With Arimoclomol in US Patients With NPC

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Summary

The document reports an Early Access Program update for arimoclomol in US patients with Niemann-Pick Disease Type C. It describes ongoing access to arimoclomol …

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Diseases / indications

• Niemann-pick Disease Type

Drugs mentioned

• Arimoclomol (arimoclomol)

Snippet

Sponsor: ZevraDenmark | Conditions: Niemann-Pick Disease, Type C | Status: AVAILABLE