EMA
approval
· 2025-10-23
EMA Authorised: Vimizim (recombinant human n-acetylgalactosamine-6-sulfatase) — BioMarin International Limited
Summary
The European Medicines Agency authorised Vimizim for the treatment of Mucopolysaccharidosis IVA (Morquio A) in 2021; Vimizim is an enzyme replacement therapy.
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Diseases / indications
Drugs mentioned
Snippet
Status: Authorised. Therapeutic area: Mucopolysaccharidosis IV. MAH: BioMarin International Limited. Decision date: 09/04/2021