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EMA approval · 2025-10-23

EMA Authorised: Vimizim (recombinant human n-acetylgalactosamine-6-sulfatase) — BioMarin International Limited

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Summary

The European Medicines Agency authorised Vimizim for the treatment of Mucopolysaccharidosis IVA (Morquio A) in 2021; Vimizim is an enzyme replacement therapy.

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Diseases / indications

Drugs mentioned

  • VIMIZIM (Elosulfase alfa)

Snippet

Status: Authorised. Therapeutic area: Mucopolysaccharidosis IV. MAH: BioMarin International Limited. Decision date: 09/04/2021