EMA Authorised: Aqneursa (L-acetylleucine) — Intrabio Ireland Limited

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Summary

The European Medicines Agency authorised Aqneursa (L-acetylleucine) by Intrabio Ireland Limited for Niemann-Pick disease, type C; it is designated an orphan med…

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Diseases / indications

• Niemann-pick Disease Type

Drugs mentioned

• AQNEURSA (LEVACETYLLEUCINE)

Snippet

Status: Authorised. Therapeutic area: Niemann-Pick Disease, Type C. MAH: Intrabio Ireland Limited. Decision date: 11/02/2026. Orphan medicine