First treatment for rare thymidine kinase 2 deficiency

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Summary

The European Medicines Agency approved Kygevvi as the first treatment for thymidine kinase 2 deficiency, with reported improvements in motor function for patien…

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Diseases / indications

• Mitochondrial Dna Depletion Syndrome Type
• Thymidine Kinase Deficiency

Drugs mentioned

• KYGEVVI (DOXECITINE AND DOXRIBTIMINE)

Snippet

Kygevvi improves motor function of patients with disease onset at or before 12 years of age