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CLINICAL_TRIALS research · 2026-04-16

Clinical Trial Update: Study to Assess the Pharmacokinetics, Safety, and Tolerability of Iptacopan in Pediatric PNH Patients [Phase 3]

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Summary

Phase 3 study to assess the pharmacokinetics, safety, and tolerability of iptacopan in pediatric patients with paroxysmal nocturnal hemoglobinuria. The study is…

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Diseases / indications

Drugs mentioned

  • iptacopan (iptacopan)

Snippet

Sponsor: Novartis Pharmaceuticals | Conditions: Paroxysmal Nocturnal Hemoglobinuria (PNH) | Phase 3 | Status: RECRUITING