CLINICAL_TRIALS
research
· 2026-04-16
Clinical Trial Update: Study to Assess the Pharmacokinetics, Safety, and Tolerability of Iptacopan in Pediatric PNH Patients [Phase 3]
Summary
Phase 3 study to assess the pharmacokinetics, safety, and tolerability of iptacopan in pediatric patients with paroxysmal nocturnal hemoglobinuria. The study is…
Upgrade for the full analysis, importance score, and drug timeline.
Diseases / indications
Drugs mentioned
Snippet
Sponsor: Novartis Pharmaceuticals | Conditions: Paroxysmal Nocturnal Hemoglobinuria (PNH) | Phase 3 | Status: RECRUITING