CLINICAL_TRIALS
trial_result
· 2026-04-16
Clinical Trial Update: Clinical Trial to Evaluate the Efficacy of Gene Therapy for Pyruvate Kinase Deficiency [Phase 2]
Summary
A Phase 2 clinical trial evaluating a Rocket Pharmaceuticals gene therapy for Pyruvate Kinase Deficiency has been suspended.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Rocket Pharmaceuticals Inc. | Conditions: Pyruvate Kinase Deficiency | Phase 2 | Status: SUSPENDED