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CLINICAL_TRIALS trial_result · 2026-04-16

Clinical Trial Update: Clinical Trial to Evaluate the Efficacy of Gene Therapy for Pyruvate Kinase Deficiency [Phase 2]

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Summary

A Phase 2 clinical trial evaluating a Rocket Pharmaceuticals gene therapy for Pyruvate Kinase Deficiency has been suspended.

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Diseases / indications

Drugs mentioned

  • Rocket PKD Gene Therapy

Snippet

Sponsor: Rocket Pharmaceuticals Inc. | Conditions: Pyruvate Kinase Deficiency | Phase 2 | Status: SUSPENDED