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CLINICAL_TRIALS research · 2026-04-16

Clinical Trial Update: A Phase 1, Dose Escalation Trial of RP-A601 in Subjects With PKP2 Variant-Mediated Arrhythmogenic Cardiomyopathy (PKP2-ACM) [Phase 1]

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Summary

Phase 1, dose-escalation study of RP-A601 in PKP2 variant-mediated arrhythmogenic cardiomyopathy is currently recruiting.

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Diseases / indications

Drugs mentioned

  • RP-A601

Snippet

Sponsor: Rocket Pharmaceuticals Inc. | Conditions: PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM) | Phase 1 | Status: RECRUITING