CLINICAL_TRIALS
research
· 2026-04-16
Clinical Trial Update: A Phase 1, Dose Escalation Trial of RP-A601 in Subjects With PKP2 Variant-Mediated Arrhythmogenic Cardiomyopathy (PKP2-ACM) [Phase 1]
Summary
Phase 1, dose-escalation study of RP-A601 in PKP2 variant-mediated arrhythmogenic cardiomyopathy is currently recruiting.
Upgrade for the full analysis, importance score, and drug timeline.
Diseases / indications
Drugs mentioned
Snippet
Sponsor: Rocket Pharmaceuticals Inc. | Conditions: PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM) | Phase 1 | Status: RECRUITING