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CLINICAL_TRIALS research · 2026-04-17

Clinical Trial Update: An Extension Study to Assess Long-Term Safety of Eplontersen in Adults With Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR-CM) [Phase 3]

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Summary

An extension study to evaluate the long-term safety of eplontersen in adults with transthyretin-mediated amyloid cardiomyopathy (ATTR-CM); it is a Phase 3 trial…

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Diseases / indications

Drugs mentioned

  • Eplontersen (eplontersen)

Snippet

Sponsor: Ionis Pharmaceuticals, Inc. | Conditions: Transthyretin-Mediated Amyloid Cardiomyopathy (ATTR CM) | Phase 3 | Status: ENROLLING_BY_INVITATION