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CLINICAL_TRIALS trial_result · 2026-04-17

Clinical Trial Update: Donidalorsen Treatment in Children With Hereditary Angioedema [Phase 3]

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Summary

Phase 3 trial evaluating donidalorsen for hereditary angioedema in children is currently recruiting.

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Diseases / indications

Drugs mentioned

  • Donidalorsen (antisense oligonucleotide targeting prekallikrein)

Snippet

Sponsor: Ionis Pharmaceuticals, Inc. | Conditions: Hereditary Angioedema (HAE) | Phase 3 | Status: RECRUITING