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CLINICAL_TRIALS research · 2026-04-20

Clinical Trial Update: Phase 3 Efficacy Study With Concurrent Control of IT MELPIDA in SPG50.Concurrent Controls. [Phase 3]

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Summary

A Phase 3 efficacy trial of IT MELPIDA for hereditary spastic paraplegia type 50 is currently recruiting, using concurrent controls.

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Diseases / indications

Drugs mentioned

  • IT MELPIDA

Snippet

Sponsor: Elpida Therapeutics SPC | Conditions: Hereditary Spastic Paraplegia Type 50 | Phase 3 | Status: RECRUITING