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CLINICAL_TRIALS research · 2026-04-20

Clinical Trial Update: A Natural History Study of Patients With GNE Myopathy and GNE-Related Diseases

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Summary

A completed natural history observational study of patients with GNE myopathy and related GNE disorders.

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Diseases / indications

Snippet

Sponsor: National Human Genome Research Institute (NHGRI) | Conditions: GNE Myopathy, GNE Related Diseases | Status: COMPLETED