Clinical Trial Update: Assessing the Safety, Tolerability, and Efficacy of APR-2020 in Pediatric and Adolescent Subjects With RPS19 Deficient Diamond-Blackfan Anemia [Phase 1]

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Summary

Phase 1 clinical trial evaluating the safety, tolerability, and preliminary efficacy of APR-2020 in children and adolescents with RPS19-deficient Diamond-Blackf…

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Diseases / indications

• Diamond-blackfan Anemia

Drugs mentioned

• APR-2020

Snippet

Sponsor: Apriligen, Inc. | Conditions: RPS19 Deficient Diamond-Blackfan Anemia | Phase 1 | Status: RECRUITING