CLINICAL_TRIALS
research
· 2026-04-21
Clinical Trial Update: Intrathecal Administration of scAAV9/JeT-GAN for the Treatment of Giant Axonal Neuropathy [Phase 1]
Summary
Phase 1 clinical trial evaluating intrathecal delivery of scAAV9/JeT-GAN for Giant Axonal Neuropathy. Status: active but not recruiting.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: National Institute of Neurological Disorders and Stroke (NINDS) | Conditions: Giant Axonal Neuropathy, Gene Transfer | Phase 1 | Status: ACTIVE_NOT_RECRUITING