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CLINICAL_TRIALS research · 2026-04-21

Clinical Trial Update: Intrathecal Administration of scAAV9/JeT-GAN for the Treatment of Giant Axonal Neuropathy [Phase 1]

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Summary

Phase 1 clinical trial evaluating intrathecal delivery of scAAV9/JeT-GAN for Giant Axonal Neuropathy. Status: active but not recruiting.

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Diseases / indications

Drugs mentioned

  • scAAV9/JeT-GAN

Snippet

Sponsor: National Institute of Neurological Disorders and Stroke (NINDS) | Conditions: Giant Axonal Neuropathy, Gene Transfer | Phase 1 | Status: ACTIVE_NOT_RECRUITING