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CLINICAL_TRIALS research · 2026-04-22

Clinical Trial Update: A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy [Phase 2]

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Summary

This document reports a Phase 2 clinical trial evaluating ARGX-119 administered intravenously in children aged 5 to under 18 with Spinal Muscular Atrophy, focus…

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Diseases / indications

Drugs mentioned

  • ARGX-119

Snippet

Sponsor: argenx | Conditions: Spinal Muscular Atrophy (SMA) | Phase 2 | Status: RECRUITING