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CLINICAL_TRIALS research · 2026-04-22

Clinical Trial Update: Alpelisib in Pediatric and Adult Patients With Lymphatic Malformations Associated With a PIK3CA Mutation. [Phase 2, Phase 3]

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Summary

A Phase 2/3 trial evaluates alpelisib for lymphatic malformations associated with PIK3CA mutations in pediatric and adult patients; recruitment is ongoing.

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Diseases / indications

Drugs mentioned

  • Piqray (alpelisib)

Snippet

Sponsor: Novartis Pharmaceuticals | Conditions: Lymphatic Malformations | Phase 2, Phase 3 | Status: RECRUITING