Clinical Trial Update: A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease (NPC) [Phase 3]

View source ↗

Summary

Phase 3 study evaluating the safety and efficacy of oral nizubaglustat (AZ-3102) in late-infantile and juvenile forms of Niemann-Pick disease type C, currently …

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

• Niemann-pick Disease Type

Drugs mentioned

• Nizubaglustat (AZ-3102) (Nizubaglustat)

Snippet

Sponsor: Azafaros A.G. | Conditions: Niemann-Pick Type C Disease | Phase 3 | Status: RECRUITING