CLINICAL_TRIALS
research
· 2026-04-23
Clinical Trial Update: Pyruvate Kinase Deficiency Global Longitudinal Registry
Summary
A global longitudinal registry for Pyruvate Kinase Deficiency sponsored by Agios Pharmaceuticals, with the study currently active but not recruiting.
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Diseases / indications
Snippet
Sponsor: Agios Pharmaceuticals, Inc. | Conditions: Pyruvate Kinase Deficiency | Status: ACTIVE_NOT_RECRUITING