Clinical Trial Update: A Study of SmartFlow Magnetic Resonance (MR) Compatible Ventricular Cannula for Administering Eladocagene Exuparvovec to Pediatric Participants [Phase 2]

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Summary

This update covers a Phase 2 study evaluating the SmartFlow MR-compatible ventricular cannula for delivering eladocagene exuparvovec in pediatric participants w…

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Diseases / indications

• Aadc Deficiency

Drugs mentioned

• Upstaza (eladocagene exuparvovec)

Snippet

Sponsor: PTC Therapeutics | Conditions: AADC Deficiency | Phase 2 | Status: ACTIVE_NOT_RECRUITING | Results posted: 2025-01-01