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CLINICAL_TRIALS research · 2026-04-24

Clinical Trial Update: A Safety and Efficacy Study of GTX-102 in Subjects With Deletion- or Nondeletion-type Angelman Syndrome (AS) [Phase 2]

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Summary

Phase 2 clinical trial update for GTX-102 in Angelman Syndrome, currently recruiting.

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Diseases / indications

Drugs mentioned

  • GTX-102

Snippet

Sponsor: Ultragenyx Pharmaceutical Inc | Conditions: Angelman Syndrome | Phase 2 | Status: RECRUITING