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CLINICAL_TRIALS research · 2026-04-24

Clinical Trial Update: A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants [Phase 3]

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Summary

This is a Phase 3 clinical trial update for migalastat in pediatric subjects aged 2 to under 12 with Fabry disease and amenable GLA variants. The study is curre…

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Diseases / indications

Drugs mentioned

  • Migalastat (migalastat)

Snippet

Sponsor: Amicus Therapeutics | Conditions: Fabry Disease | Phase 3 | Status: RECRUITING