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CLINICAL_TRIALS withdrawal · 2025-10-20

Clinical Trial Update: Compassionate Use of Pozelimab and Cemdisiran Combination Therapy in Patients With Paroxysmal Nocturnal Hemoglobinuria

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Summary

The clinical trial update indicates that compassionate-use access to the pozelimab and cemdisiran combination therapy for Paroxysmal nocturnal hemoglobinuria is…

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Diseases / indications

Drugs mentioned

  • Cemdisiran (cemdisiran)
  • Pozelimab

Snippet

Sponsor: Regeneron Pharmaceuticals | Conditions: Paroxysmal Nocturnal Hemoglobinuria | Status: NO_LONGER_AVAILABLE