Clinical Trial Update: Gene Therapy For Children With Variant Late Infantile Neuronal Ceroid Lipofuscinosis 6 (vLINCL6) Disease [Phase 1, Phase 2]

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Summary

This clinical trial update reports results from Phase 1/2 testing of a gene therapy for children with variant late-infantile neuronal ceroid lipofuscinosis type…

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Diseases / indications

• Variant Late-infantile Neuronal Ceroid Lipofuscinosis

Snippet

Sponsor: Emily de los Reyes | Conditions: Variant Late-Infantile Neuronal Ceroid Lipofuscinosis | Phase 1, Phase 2 | Status: COMPLETED | Results posted: 2023-03-08