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CLINICAL_TRIALS trial_result · 2025-10-24

Clinical Trial Update: Natural History Study of Infantile and Juvenile GM1 Gangliosidosis (GM1) Patients

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Summary

This clinical trial update reports that the natural history study of GM1 Gangliosidosis in infantile and juvenile patients has completed. It will provide observ…

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Diseases / indications

Snippet

Sponsor: University of Pennsylvania | Conditions: GM1 Gangliosidosis | Status: COMPLETED