Clinical Trial Update: A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice

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Summary

This clinical trial update describes the natural history of participants with LGMD subtypes 2A/R1, 2C/R5, 2D/R3, and 2E/R4 aged 4 years and older who are manage…

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Diseases / indications

• Limb Girdle Muscular Dystrophy

Snippet

Sponsor: Sarepta Therapeutics, Inc. | Conditions: Limb-girdle Muscular Dystrophy | Status: ACTIVE_NOT_RECRUITING