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CLINICAL_TRIALS research · 2025-11-10

Clinical Trial Update: DFT383 in Pediatric Participants With Nephropathic Cystinosis [Phase 1, Phase 2]

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Summary

DFT383 is being studied in pediatric participants with nephropathic cystinosis in Phase 1/2 trials. The study is currently recruiting, sponsored by Novartis Pha…

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Diseases / indications

Drugs mentioned

  • DFT383

Snippet

Sponsor: Novartis Pharmaceuticals | Conditions: Nephropathic Cystinosis | Phase 1, Phase 2 | Status: RECRUITING