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CLINICAL_TRIALS trial_result · 2025-11-13

Clinical Trial Update: Study of Safety, Tolerability and Efficacy of PBKR03 in Pediatric Subjects With Early Infantile Krabbe Disease [Phase 1, Phase 2]

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Summary

The clinical trial update indicates the Phase 1/2 study of PBKR03 in pediatric subjects with Krabbe disease is currently suspended.

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Diseases / indications

Drugs mentioned

  • PBKR03

Snippet

Sponsor: Gemma Biotherapeutics | Conditions: Leukodystrophy, Globoid Cell | Phase 1, Phase 2 | Status: SUSPENDED