Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS research · 2025-11-14

Clinical Trial Update: Gene Editing For Sickle Cell Disease [Phase 1]

View source ↗

Summary

A Phase 1 clinical trial led by St. Jude Children's Research Hospital is evaluating a gene editing approach for sickle cell disease and is currently recruiting.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Snippet

Sponsor: St. Jude Children's Research Hospital | Conditions: Sickle Cell Disease | Phase 1 | Status: RECRUITING