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CLINICAL_TRIALS research · 2025-11-14

Clinical Trial Update: A Multi-Country Observational Study of Safety and Effectiveness of Elfabrio® in Fabry Patients

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Summary

A multi-country observational study evaluating the safety and effectiveness of Elfabrio (migalastat) in Fabry disease patients, sponsored by Chiesi Farmaceutici…

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Diseases / indications

Drugs mentioned

  • Elfabrio (migalastat)

Snippet

Sponsor: Chiesi Farmaceutici S.p.A. | Conditions: Fabry Disease | Status: RECRUITING