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CLINICAL_TRIALS trial_result · 2025-12-04

Clinical Trial Update: A Study to Investigate the Pharmacokinetics (PK) and Safety and to Provide Proof of Mechanism of Alogabat in Children and Adolescents Aged 5-17 Years With Angelman Syndrome (AS) With Deletion Genotype. [Phase 2]

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Summary

Phase 2 study evaluating the pharmacokinetics, safety, and mechanism of action of alogabat in children and adolescents with Angelman syndrome with deletion geno…

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Diseases / indications

Drugs mentioned

  • Alogabat (alogabat)

Snippet

Sponsor: Hoffmann-La Roche | Conditions: Angelman Syndrome | Phase 2 | Status: COMPLETED