CLINICAL_TRIALS
trial_result
· 2025-12-04
Clinical Trial Update: A Study to Investigate the Pharmacokinetics (PK) and Safety and to Provide Proof of Mechanism of Alogabat in Children and Adolescents Aged 5-17 Years With Angelman Syndrome (AS) With Deletion Genotype. [Phase 2]
Summary
Phase 2 study evaluating the pharmacokinetics, safety, and mechanism of action of alogabat in children and adolescents with Angelman syndrome with deletion geno…
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Sponsor: Hoffmann-La Roche | Conditions: Angelman Syndrome | Phase 2 | Status: COMPLETED