Clinical Trial Update: Study of DNL126 in Pediatric Participants With Mucopolysaccharidosis Type IIIA (Sanfilippo Syndrome Type A) [Phase 1, Phase 2]

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Summary

Update on a Phase 1/2 clinical trial of DNL126 in pediatric patients with Mucopolysaccharidosis Type IIIA (Sanfilippo syndrome type A); the study is active but …

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Diseases / indications

• Mucopolysaccharidosis Type Iiia
• Sanfilippo Syndrome Type

Drugs mentioned

• DNL126

Snippet

Sponsor: Denali Therapeutics Inc. | Conditions: Mucopolysaccharidosis Type IIIA | Phase 1, Phase 2 | Status: ACTIVE_NOT_RECRUITING