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CLINICAL_TRIALS research · 2025-12-10

Clinical Trial Update: A Randomized, Parallel-arm, Double Blind, Placebo-controlled Study to Assess the Efficacy of Fampridine for Patients With Spinocerebellar Ataxia SCA27B Caused by a GAA Expansion in the FGF14 Gene [Phase 3]

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Summary

A Phase 3 randomized, double-blind, placebo-controlled trial is evaluating fampridine for spinocerebellar ataxia type 27B due to an FGF14 gene expansion. Recrui…

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Diseases / indications

Drugs mentioned

  • Fampridine (4-aminopyridine)

Snippet

Sponsor: Assistance Publique - Hôpitaux de Paris | Conditions: Spinocerebellar Ataxia 27B (SCA27B) | Phase 3 | Status: RECRUITING