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CLINICAL_TRIALS research · 2025-12-11

Clinical Trial Update: Randomized Stepped Wedge Study of Emapalumab in APECED Enteritis [Phase 2]

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Summary

Phase 2 randomized stepped-wedge trial evaluating emapalumab for enteritis in Autoimmune Polyendocrinopathy Candidiasis Ectodermal Dystrophy (APECED).

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Diseases / indications

Drugs mentioned

  • GAMIFANT (emapalumab-lzsg)

Snippet

Sponsor: National Institute of Allergy and Infectious Diseases (NIAID) | Conditions: Autoimmune Polyendocrinopathy Candidiasis Ectodermal Dystrophy Enteritis | Phase 2 | Status: RECRUITING