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CLINICAL_TRIALS research · 2025-12-11

Clinical Trial Update: Safety and Preliminary Efficacy of VG801 in Patients With ABCA4 Mutation-associated Retinal Dystrophy (Stargardt Disease) [Phase 1, Phase 2]

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Summary

Clinical trial update on VG801 for Stargardt disease due to ABCA4 mutations, reporting safety assessments and preliminary efficacy signals from Phase 1/2 while …

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Diseases / indications

Drugs mentioned

  • VG801

Snippet

Sponsor: VeonGen Therapeutics GmbH | Conditions: Retinal Dystrophy Due to Biallelic ABCA4 Mutations, Stargardt Disease 1 | Phase 1, Phase 2 | Status: RECRUITING